Eplontersen

• CAT Number: I042893
• CAS Number: 1637600-16-8
• Molecular Weight: 8606.50
• Purity: ≥95%

Eplontersen（Cat No.:I042893）is an investigational antisense oligonucleotide therapy designed to treat hereditary transthyretin amyloidosis (hATTR), a rare genetic disorder caused by misfolded transthyretin proteins that accumulate in tissues, leading to organ damage. Eplontersen works by targeting and inhibiting the production of abnormal transthyretin (TTR) proteins, thereby reducing amyloid deposits and preventing further damage to organs like the heart and nerves. In clinical trials, Eplontersen has shown promise in improving clinical outcomes, slowing disease progression, and providing relief from symptoms. It is being evaluated as a potential treatment option for patients with hATTR.