For research use only. Not for therapeutic Use.
GCase Activator 2(Cat No.:I041060)is a small molecule designed to enhance the activity of glucocerebrosidase (GCase), an enzyme involved in the breakdown of glucocerebroside. By increasing GCase activity, it helps to address the accumulation of glucocerebroside in lysosomes, a hallmark of Gaucher disease and other lysosomal storage disorders. GCase Activator 2 is being investigated for its potential to improve cellular function, reduce substrate buildup, and offer therapeutic benefits in treating these diseases. Its ability to activate GCase holds promise for enhancing lysosomal enzyme replacement therapies.
CAS Number | 2759897-35-1 |
Synonyms | 1-[4-[2-(4-methoxyphenyl)-5-methylpyrrolo[2,3-b]pyrazin-6-yl]piperidin-1-yl]ethanone |
Molecular Formula | C21H24N4O2 |
Purity | ≥95% |
IUPAC Name | 1-[4-[2-(4-methoxyphenyl)-5-methylpyrrolo[2,3-b]pyrazin-6-yl]piperidin-1-yl]ethanone |
InChI | InChI=1S/C21H24N4O2/c1-14(26)25-10-8-16(9-11-25)20-12-18-21(24(20)2)22-13-19(23-18)15-4-6-17(27-3)7-5-15/h4-7,12-13,16H,8-11H2,1-3H3 |
InChIKey | HEAGFUMRBLFGAD-UHFFFAOYSA-N |
SMILES | CC(=O)N1CCC(CC1)C2=CC3=NC(=CN=C3N2C)C4=CC=C(C=C4)OC |